GOP Sen. Johnson Probes FDA Rare Disease Rejections

Sen. Ron Johnson (R-WI) launches a probe into the FDA's outrageous rejections of rare disease therapies, demanding complete response letters to expose the bureaucratic roadblocks killing patient hope. He's slamming the agency's demand for a sham surgery-controlled Phase 3 trial for uniQure's Huntington's gene therapy AMT-130 as "bureaucratic idiocy," especially after it showed 75% slowed progression in trials. Read more about this...